Clinical Trials

To learn more about current and past clinical trials, please visit 

Raising a Hand
for Rett - The Book to present to rsam in march 2018

Dr. Steve Kaminsky and Gordon Rich of will be visiting Boston in March (date/location TBD) to update us on the current status of Rett research.  All are invited.  More details to be available shortly.

Triheptanoin (UX007) Clinical Trial Currently Recruiting 10 Participants

Dr. Daniel Tarquinio, director of the Rett Syndrome Clinic in Atlanta, is currently recruiting a 10-person, open label trail (everyone will recieve the drug.  
Visit for more information and contact Dr. Daniel Tarquinio at 

Families helping Families living with Rett Syndrome

Donate Today

At Rett Syndrome Association of Massachusetts, Inc. we are working to create hope and the opportunity for a better world. But we can only do it with your help. Join with us in our mission and donate now. 

Rett Syndrome Program,
​Children's Hospital Boston

The Rett Syndrome Program at Children’s Hospital Boston is the only specialist Rett syndrome program in New England. CHB sees more than 250 patients who have Rett syndrome and related disorders.

Specialized Treatment
The physical symptoms of Rett syndrome, such as seizures, gastrointestinal problems and musculoskeletal problems, can often be alleviated and managed. The Rett Program brings together Children's physicians and therapists who are experienced in caring for children and adults with Rett syndrome. 

David Lieberman, MD, PhD
Rett Syndrome Program
Children's Hospital Boston/Harvard Medical School
Fegan 11
300 Longwood Avenue
Boston, MA 02115